Funding Rare Disease Therapies in Australia

Ensuring equitable access to health care for all Australians

A rare disease is a life threatening or chronically debilitating condition that only affects a very small number of people in the population. Any therapy developed to treat a rare disease thus only has a very limited number of potential patients.

This report sets out the current Australian policy for funding rare disease therapies and considers this in the context of Australia’s universal health care system.

The report concludes with a proposed way forward, including recommended principles to guide the development of future rare disease policy in Australia.

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